Casgevy: UK approves gene-editing drug for blood disorders
Medical regulators approve a gene therapy that aims to cure sickle cell disease and beta thalassemia. Source link
Medical regulators approve a gene therapy that aims to cure sickle cell disease and beta thalassemia. Source link
The new rules close the loopholes that enabled Dr He to evade regulations, which previously only applied to experiments on human beings in hospitals, for example for drug trials. The updated regulations cover all research institutions and everything relating to humans, including work on tissues, organs and embryonic cells. Source link
His family urged Jimi to take part in other clinical trials or have a bone marrow transplant – which is an option for some people with sickle cell. But he thought they would involve too much time in hospital for the improvement in his quality of life. Instead, he pinned his hopes on a cure … Read more