Muscular dystrophy: Child racks up 1,200 miles a month for treatment
Muscular dystrophy patient Elliot, five, makes the journey from Newport to Newcastle twice a month. Source link
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Spinal muscular atrophy: Baby heel prick test ‘could be life-changing’
An Irish mother wants babies tested at birth so those with a rare condition are treated quickly. Source link
Take at home treatment for spinal muscular atrophy
The oral drug could help children like Melvil born with a condition that causes progressive muscle weakness. Source link
Spinal muscular atrophy: Gene therapy approved by NHS
Meindert Boysen, deputy chief executive and director of the Centre for Health Technology Evaluation at Nice, said: “Spinal Muscular Atrophy is a very serious, debilitating and distressing condition that has very significant effects on every aspect of life of those with SMA, and their families and carers. Source link